> Trialight public data. Index of pages: https://trialight.com/llms.txt
> Web page: https://trialight.com/data/condition/becker-muscular-dystrophy-2f7ee208-5e4f-5487-a152-945506d1f5d0
> Record changed: 2026-11-04

# Becker muscular dystrophy

Therapeutic area

Neurology

Rare disease

Yes

## Definition and classification

**Definition**

Becker muscular dystrophy (BMD) is a neuromuscular disease characterized by progressive muscle wasting and weakness due to degeneration of skeletal, smooth and cardiac muscle.

**Genetic basis**

Yes

**Non-human condition**

No

**Rare disease**

Yes

**Listing at source**

Listed

**Condition name**

Becker muscular dystrophy

**Therapeutic area**

Neurology

### Alternative names (8)

- Becker muscular dystrophy
- Becker dystrophinopathy
- Becker muscular dystrophy, X-linked recessive
- Becker's Muscular Dystrophy
- BMD
- Duchenne and Becker Muscular Dystrophy
- muscular dystrophy pseudohypertrophic progressive, Becker type
- muscular dystrophy, Becker type

## Clinical profile

**Severity**

Severe

### Disease mechanisms (2)

- Genetic
- Hereditary

Sources for recorded values

Source: [monarchinitiative.org](https://monarchinitiative.org/MONDO:0010311)

### All therapeutic areas (3)

- Neurology
- Neuromuscular Disease
- Rheumatology

Sources for recorded values

Source: [monarchinitiative.org](https://monarchinitiative.org/MONDO:0010311)

## Identifiers

**MONDO ID**

MONDO:0010311

Source: [monarchinitiative.org](https://monarchinitiative.org/MONDO:0010311)

**Parent condition**

MONDO:0700285

## Related records

### Broader conditions (17)

- Disease
- Disease by body system or component
- Disease by etiologic mechanism
- Disease of genetic or genomic mechanism
- DMD-related muscular dystrophy
- [Hereditary disease](https://trialight.com/data/condition/hereditary-disease-df2f8f05-e0c9-5777-8e51-c3b6639743d3.md)
- Hereditary neurological disease
- Hereditary neuromuscular disease
- Hereditary skeletal muscle disorder
- Human disease
- Muscle tissue disorder
- Muscular dystrophy
- [Musculoskeletal system disorder](https://trialight.com/data/condition/musculoskeletal-system-disorder-16f6e157-12a0-54ee-9e24-377731f344a5.md)
- Myopathy
- [Nervous system disorder](https://trialight.com/data/condition/nervous-system-disorder-541eb3ed-9656-574d-babf-28139b060a42.md)
- Neuromuscular disease
- Skeletal muscle disorder

### Narrower conditions (1)

- Muscular dystrophy, pseudohypertrophic, with Internalized capillaries

### Trials (59)

- (-)- Epicatechin Becker Muscular Dystrophy
- A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese Children
- A Study of EDG-5506 in Adult Males With Becker Muscular Dystrophy
- A Study to Assess Safety, Tolerability, and PK of EDG-5506 in Healthy Volunteers and Becker Muscular Dystrophy Adults
- A Study to Assess Vamorolone in Becker Muscular Dystrophy (BMD)
- Applying the Pathways and Resources for Engagement and Participation Protocol Among People With Muscles Dystrophies
- Becker Muscular Dystrophy - A Natural History Study to Predict Efficacy of Exon Skipping
- Biomarker Development for Muscular Dystrophies
- Brain Involvement in Dystrophinopathies Part 1
- Brain Involvement in Dystrophinopathies Part 2
- Cardiac Magnetic Resonance in Children With Muscular Dystrophy
- Cardiac Outcome Measures in Children With Muscular Dystrophy
- Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMD
- Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Becker Muscular Dystrophy
- Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies
- CRD007 for the Treatment of Duchenne Muscular Dystrophy, Becker Muscular Dystrophy and Symptomatic Carriers
- CureDuchenne Link®: A Resource for Research
- Defining Endpoints in Becker Muscular Dystrophy
- Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
- DMD Gene Variants and Cardiac Dysfunction in Young Males With Dystrophinopathies

### Approved drugs (3)

- Ataluren
- Delandistrogene moxeparvovec
- Vamorolone

### Drugs in development (16)

- (-)-epicatechin Phase 2
- (+)-epicatechin Phase 1
- Enalapril Phase 3
- [Filgrastim](https://trialight.com/data/asset/filgrastim-942bf0d3-0bf1-4bf8-9e38-81a6c277d728.md) Phase 1
- Gentamicin Phase 1
- Givinostat Phase 3
- L-citrulline Phase 2
- [Metformin](https://trialight.com/data/asset/metformin-0292cbe3-3a2f-4db7-b783-270ef048c3b4.md) Phase 2
- Pemirolast Phase 2
- Pemirolast potassium Phase 2
- [Prednisone](https://trialight.com/data/asset/prednisone-a5a99f90-5fbe-45c2-a625-34ba78735da6.md) Phase 2
- [Sevasemten](https://trialight.com/data/asset/sevasemten-640936ae-ecc4-486d-bb36-40e23e0f1ef2.md) Phase 2
- Sildenafil Phase 2
- Sodium nitrate Phase 2
- Stamulumab Phase 1
- [Tadalafil](https://trialight.com/data/asset/tadalafil-4b34b94f-a4f3-4c9a-a187-9910e81423ab.md) Phase 1

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