Becker muscular dystrophy
Therapeutic area
Neurology
Rare disease
Yes
- Definition
- Becker muscular dystrophy (BMD) is a neuromuscular disease characterized by progressive muscle wasting and weakness due to degeneration of skeletal, smooth and cardiac muscle.
- Genetic basis
- Yes
- Non-human condition
- No
- Rare disease
- Yes
- Listing at source
- Listed
- Condition name
- Becker muscular dystrophy
- Therapeutic area
- Neurology
- Becker muscular dystrophy
- Becker dystrophinopathy
- Becker muscular dystrophy, X-linked recessive
- Becker's Muscular Dystrophy
- BMD
- Duchenne and Becker Muscular Dystrophy
- muscular dystrophy pseudohypertrophic progressive, Becker type
- muscular dystrophy, Becker type
- Severity
- Severe
- Genetic
- Hereditary
Sources for recorded values
- Neurology
- Neuromuscular Disease
- Rheumatology
Sources for recorded values
- MONDO ID
- MONDO:0010311
- Parent condition
- MONDO:0700285
Related records
Broader conditions (17)
- Disease
- Disease by body system or component
- Disease by etiologic mechanism
- Disease of genetic or genomic mechanism
- DMD-related muscular dystrophy
- Hereditary disease
- Hereditary neurological disease
- Hereditary neuromuscular disease
- Hereditary skeletal muscle disorder
- Human disease
- Muscle tissue disorder
- Muscular dystrophy
- Musculoskeletal system disorder
- Myopathy
- Nervous system disorder
- Neuromuscular disease
- Skeletal muscle disorder
Narrower conditions (1)
- Muscular dystrophy, pseudohypertrophic, with Internalized capillaries
Trials (59)
- (-)- Epicatechin Becker Muscular Dystrophy
- A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese Children
- A Study of EDG-5506 in Adult Males With Becker Muscular Dystrophy
- A Study to Assess Safety, Tolerability, and PK of EDG-5506 in Healthy Volunteers and Becker Muscular Dystrophy Adults
- A Study to Assess Vamorolone in Becker Muscular Dystrophy (BMD)
- Applying the Pathways and Resources for Engagement and Participation Protocol Among People With Muscles Dystrophies
- Becker Muscular Dystrophy - A Natural History Study to Predict Efficacy of Exon Skipping
- Biomarker Development for Muscular Dystrophies
- Brain Involvement in Dystrophinopathies Part 1
- Brain Involvement in Dystrophinopathies Part 2
- Cardiac Magnetic Resonance in Children With Muscular Dystrophy
- Cardiac Outcome Measures in Children With Muscular Dystrophy
- Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMD
- Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Becker Muscular Dystrophy
- Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies
- CRD007 for the Treatment of Duchenne Muscular Dystrophy, Becker Muscular Dystrophy and Symptomatic Carriers
- CureDuchenne Link®: A Resource for Research
- Defining Endpoints in Becker Muscular Dystrophy
- Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
- DMD Gene Variants and Cardiac Dysfunction in Young Males With Dystrophinopathies
Approved drugs (3)
- Ataluren
- Delandistrogene moxeparvovec
- Vamorolone
Drugs in development (16)
- (-)-epicatechin Phase 2
- (+)-epicatechin Phase 1
- Enalapril Phase 3
- Filgrastim Phase 1
- Gentamicin Phase 1
- Givinostat Phase 3
- L-citrulline Phase 2
- Metformin Phase 2
- Pemirolast Phase 2
- Pemirolast potassium Phase 2
- Prednisone Phase 2
- Sevasemten Phase 2
- Sildenafil Phase 2
- Sodium nitrate Phase 2
- Stamulumab Phase 1
- Tadalafil Phase 1