> Trialight public data. Index of pages: https://trialight.com/llms.txt
> Web page: https://trialight.com/data/company/ptc-therapeutics-f4460a55-b956-466e-8546-765ac5587bce
> Record changed: 2026-10-13

# PTC Therapeutics

Headquarters country

United States

Source: [search.gleif.org](https://search.gleif.org/#/record/549300UJLWOIWFDGB318)

Registry sponsor category

Industry

Source: [clinicaltrials.gov](https://clinicaltrials.gov/)

## Names and classification

**Other names**

- PTC Therapeutics

**Company name**

PTC Therapeutics

**Organisation type**

Industry

**Registered legal name**

PTC THERAPEUTICS, INC.

Source: [search.gleif.org](https://search.gleif.org/#/record/549300UJLWOIWFDGB318)

**US industry code (SIC)**

Pharmaceutical preparations

Source: [www.sec.gov](https://www.sec.gov/cgi-bin/browse-edgar?action=getcompany&CIK=0001070081)

**Registry sponsor category**

Industry

Source: [clinicaltrials.gov](https://clinicaltrials.gov/)

**Website**

http://www.ptcbio.com/en/

Source: [www.wikidata.org](https://www.wikidata.org/wiki/Q7120959)

## Location and listing

**Headquarters country**

United States

Source: [search.gleif.org](https://search.gleif.org/#/record/549300UJLWOIWFDGB318)

**Publicly traded (proxy)**

Yes

**Listing at source**

Listed

## Identifiers

**SEC filer number (CIK)**

0001070081

Source: [www.sec.gov](https://www.sec.gov/cgi-bin/browse-edgar?action=getcompany&CIK=0001070081)

**Legal Entity Identifier (LEI)**

549300UJLWOIWFDGB318

Source: [search.gleif.org](https://search.gleif.org/#/record/549300UJLWOIWFDGB318)

**Wikidata ID**

Q7120959

Source: [www.wikidata.org](https://www.wikidata.org/wiki/Q7120959)

## Related records

### Trials (76)

- A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion
- A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria
- A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy
- A Phase 1b Study of PTC596 in Children With Newly Diagnosed Diffuse Intrinsic Pontine Glioma and High Grade Glioma
- A Phase 2 Open Label Extension Study in Participants With Nonsense Mutation Aniridia
- A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC
- A Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial Disease
- A Single Dose Evaluation of the Effects of Moderate Hepatic Impairment on Deflazacort Pharmacokinetics
- A Single Dose Evaluation of the Effects of Renal Impairment on Deflazacort Pharmacokinetics
- A Study of Ataluren in Pediatric Participants With Cystic Fibrosis
- A Study of CNSA-001 in Women With Diabetic Gastroparesis
- A Study of Deflazacort (Emflaza®) in Participants With Duchenne Muscular Dystrophy (DMD)
- A Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I)
- A Study of PTC923 (CNSA-001) in Primary Tetrahydrobiopterin (BH4) Deficient Participants With Hyperphenylalaninemia
- A Study of PTC923 in Participants With Phenylketonuria
- A Study of Sepiapterin in Participants With Phenylketonuria (PKU)
- A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric Participants
- A Study of Unesbulin (PTC596) in Combination With Dacarbazine in Participants With Advanced Leiomyosarcoma (LMS)
- A Study of Unesbulin in Participants With Advanced Leiomyosarcoma (LMS)
- A Study of Vatiquinone for the Treatment of Participants With Friedreich Ataxia

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